Search for Clinical Trial Results
Niemann-Pick Disease Type C1 - 25 Studies Found
Status | Study |
Completed |
Study Name: Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine Condition: Niemann-Pick Disease, Type C Date: 2009-09-10 Interventions: Drug: N-Acetyl Cysteine 900mg effervescent tablet; Dosed as 15 mg/kg/day (maximum dose 900 mg per day) f |
Completed |
Study Name: Longitudinal Study of Cognition With Niemann-Pick Disease, Type C Condition: Niemann-Pick Disease, Type C Date: 2013-07-04 |
Completed |
Study Name: Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease Condition: Niemann-Pick Disease, Type C1 Date: 2012-12-08 Interventions: Drug: VTS-270 Other Name: 2-hydroxypropyl-beta-cyclodextrin |
Terminated |
Study Name: Screening of Niemann-Pick Disease, Type C in a Psychiatric Population Condition: Psychiatric Adults Patients Date: 2016-07-11 Interventions:
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Completed |
Study Name: Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1 Condition: Neimann-Pick Disease Date: 2014-04-25 Interventions: Drug: Vorinostat Histone deactylase inhibitor |
Active, not recruiting |
Study Name: Arimoclomol Prospective Study in Patients Diagnosed With NiemannPick Disease Type C Condition: Niemann-Pick Disease, Type C Date: 2015-11-12 Interventions:
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Recruiting |
Study Name: Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) to Treat Niemann-Pick Type C1 (NPC1) Disease Condition: Niemann-Pick Disease, Type C Date: 2015-08-18 Interventions:
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Completed |
Study Name: A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C Condition: Niemann-Pick Disease, Type C Date: 2015-04-22 |
Recruiting |
Study Name: Study of the Pharmacokinetics of Trappsol and Effects on Potential Biomarkers of Niemann-Pick C1 (NPC1) Condition: Niemann-Pick Disease, Type C1 Date: 2016-09-21 Interventions: Drug: Hydroxypropyl-beta-cyclodextrin Used in the treatment of Niemann-Pick Disease C1 ( NPC1) |
Recruiting |
Study Name: Study of Pharmacokinetics and Preliminary Efficacy in Patients With Niemann-Pick C1 Condition: Niemann-Pick Disease, Type C1 Date: 2016-08-19 Interventions: Drug: Hydroxypropyl-beta-cyclodextrin Used in the treatment of Niemann-Pick C1 |